GeneH: Excellence Hub for Advancing Innovation in Gene Therapy

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Programme:

Horizon Europe

The GeneH project is designed to accelerate the development and implementation of gene therapy, particularly in the field of rare genetic diseases. Its aim is to adopt a holistic approach—based on the quadruple helix model—to connect key stakeholders: research institutions, industry, healthcare professionals, regulatory bodies, and civil society. By doing so, the project lays the foundation for a more efficient translation of scientific breakthroughs into clinical practice.

Despite significant progress in research, many challenges remain: a limited number of clinical trials, complex regulatory procedures, lack of specialized infrastructure, and insufficient funding. The GeneH project seeks to address these barriers through targeted and effective measures.

Project objectives:

Interdisciplinary collaboration: Strengthening connections between scientists, industry, healthcare providers, regulators, and patients.
Research and development innovation: Aligning scientific achievements with market and societal needs.
Clinical translation: Enabling faster and safer transfer of innovations into clinical practice for real patient benefit.
Sustainable funding: Attracting public and private investments to ensure long-term stability in the gene therapy field.
Education and training: Developing programs for researchers and healthcare professionals to enhance expertise and capacity.
Regulatory compliance and ethics: Establishing robust, safe, and ethical frameworks for the development and application of new therapies.

By integrating all these dimensions, the GENEH project will make a significant contribution to the advancement of innovative solutions and strengthen Europe’s leadership in gene therapy—particularly for the benefit of patients who are still awaiting effective treatments.